Once-daily, subcutaneous vosoritide therapy in children with achondroplasia: a randomised, double-blind, phase 3, placebo-controlled, multicentre trial

dc.contributor.authorSavarirayan, Ravi
dc.contributor.authorTofts, Louise
dc.contributor.authorIrving, Melita
dc.contributor.authorWilcox, William
dc.contributor.authorBacino, Carlos A.
dc.contributor.authorHoover\\-Fong, Julie
dc.contributor.authorUllot Font, Rosendo
dc.contributor.authorHarmatz, Paul
dc.contributor.authorRutsch, Frank
dc.contributor.authorBober, Michael B.
dc.contributor.authorPolgreen, Lynda E.
dc.contributor.authorGinebreda, Ignacio
dc.contributor.authorMohnike, Klaus
dc.contributor.authorCharrow, Joel
dc.contributor.authorHoernschemeyer, Daniel
dc.contributor.authorOzono, Keiichi
dc.contributor.authorAlanay, Yasemin
dc.contributor.authorArundel, Paul
dc.contributor.authorKagami, Shoji
dc.contributor.authorYasui, Natsuo
dc.contributor.authorWhite, Klane K.
dc.contributor.authorSaal, Howard M.
dc.contributor.authorLeiva\\-Gea, Antonio
dc.contributor.authorLuna\\-Gonzalez, Felipe
dc.contributor.authorMochizuki, Hiroshi
dc.contributor.authorBasel, Donald
dc.contributor.authorPorco, Dania M.
dc.contributor.authorJayaram, Kala
dc.contributor.authorFisheleva, Elena
dc.contributor.authorHuntsman\\-Labed, Alice
dc.contributor.authorDay, Jonathan
dc.date.accessioned2025-10-16T15:20:55Z
dc.date.issued2020
dc.identifier.otherWOS:000579138700028
dc.identifier.urihttps://openaccess.acibadem.edu.tr/handle/11443/7578
dc.publisherELSEVIER SCIENCE INC
dc.sourceLANCET
dc.titleOnce-daily, subcutaneous vosoritide therapy in children with achondroplasia: a randomised, double-blind, phase 3, placebo-controlled, multicentre trial
dc.typeArticle

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